September 18–19, 2026
9 AM – 2 PM CT
ZOOM | Live Translation
Registration is free for all participants
Unparalleled Connection to a Global Network
This summit brings together a unique, global network of stakeholders:
- Leading scientists and researchers exploring cutting-edge gene therapy, drug repurposing, and other potential therapies
- Clinicians and care providers seeking the latest protocols and research insights to improve patient outcomes
- Resilient families and advocates from around the world who are the driving force behind our community